Searching for a cure for Niemann-Pick Type C - NemaMetrix

Niemann-Pick Type C is a rare and fatal disorder affecting children. We explore the efficacy of new potential therapeutics with the ScreenChip System.

Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study - The Lancet Neurology

PDF) Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-Β-Cyclodextrin

Searching for a cure for Niemann-Pick Type C - NemaMetrix

Searching for a cure for Niemann-Pick Type C - NemaMetrix

Hekimler için-Niemann Pick Tip C – Çocuk Metabolizma

Niemann Pick Disease Type C - Symptoms, Causes, Treatment

Parents of twins with Niemann-Pick find a treatment

Niemann-Pick Type C Disease

PDF) Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-Β-Cyclodextrin

Full article: New therapies in the management of Niemann-Pick type C disease: clinical utility of miglustat

Why is Niemann-Pick Type C Difficult to Treat?