Miglustat for treatment of Niemann-Pick C disease: a randomised

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Last updated 25 março 2025
Miglustat for treatment of Niemann-Pick C disease: a randomised
Miglustat for treatment of Niemann-Pick C disease: a randomised
Imaging of neuroinflammation in adult Niemann-Pick type C disease
Miglustat for treatment of Niemann-Pick C disease: a randomised
New therapies in the management of Niemann-Pick type C disease: clinical utility of miglustat
Miglustat for treatment of Niemann-Pick C disease: a randomised
Chronic Cyclodextrin Treatment of Murine Niemann-Pick C Disease Ameliorates Neuronal Cholesterol and Glycosphingolipid Storage and Disease Progression
Miglustat for treatment of Niemann-Pick C disease: a randomised
Cureus, Niemann-Pick Disease: An Approach for Diagnosis in Adulthood
Miglustat for treatment of Niemann-Pick C disease: a randomised
Rapid Diagnosis of 83 Patients with Niemann Pick Type C Disease and Related Cholesterol Transport Disorders by Cholestantriol Screening - eBioMedicine
Miglustat for treatment of Niemann-Pick C disease: a randomised
Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: a national French retrospective study, Orphanet Journal of Rare Diseases
Miglustat for treatment of Niemann-Pick C disease: a randomised
The pathogenesis of Niemann–Pick type C disease: a role for autophagy?, Expert Reviews in Molecular Medicine
Miglustat for treatment of Niemann-Pick C disease: a randomised
PDF] Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study
Miglustat for treatment of Niemann-Pick C disease: a randomised
Pharmaceutical Benefits Scheme (PBS) Miglustat, capsule, 100 mg, Zavesca® - November 2011
Miglustat for treatment of Niemann-Pick C disease: a randomised
Cost-effectiveness of miglustat versus symptomatic therapy of Niemann–Pick disease type C
Miglustat for treatment of Niemann-Pick C disease: a randomised
Miglustat, C10H21NO4
Miglustat for treatment of Niemann-Pick C disease: a randomised
Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study - The Lancet Neurology

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